English
SpanishTrusted Resources: News & Meetings
Latest announcements and gatherings
Why Some Drugs Cost $2.1 Million per Dose and how one Company Plans to Change This
With a cost of $2.1 million for a one-dose treatment, Zolgensma is currently the most expensive drug in the United States. Zolgensma treats spinal muscular atrophy (SMA), a genetic disorder that causes muscle wasting and weakness. Although the U.S. Food and Drug Administration (FDA) approved Zolgensma in 2019, some health insurance companies still do not cover it because of the high cost, and others have strict requirements that limit the number of patients who qualify for coverage.
To understand why a single dose of a drug costs $2.1 million, you have to start by looking at how it is manufactured and why it was created in the first place. Zolgensma falls into the category of personalized or precision medicine because it is a drug that targets specific problems caused by a person’s unique genetic code. Precision medicine is considered to be much more effective for treating diseases than conventional, one-size-fits-all methods.
BookmarkRelated Content
-
Combination Therapy With Nusinersen and Onasemnogene Abeparvovec-xioi in Spinal Muscular Atrophy Type ISpinal muscular atrophy (SMA) is a neuro...
-
A Caregiver’s Guide to ZolgensmaIndication ZOLGENSMA® (onasemnogene abe...
-
Infants With Symptomatic SMA Reach Milestones With Gene TherapyGene replacement therapy with onasemnoge...
-
Spinal Muscular Atrophy: From Rags to RichesThe aim of this paper is to provide a sh...
-
Lunch & Learn: Gene Therapy for SMAhttps://www.youtube.com/watch?v=YFEMR1ZH...
-
Spinal Muscular Atrophy 2020: SMA Medications for Treatment Updateshttps://www.youtube.com/watch?v=dnSXnvrO...
-
Spinal Muscular Atrophy Fact SheetWhat is spinal muscular atrophy?Spinal m...
Powered by
In partnership with
