Why Choose CHOP for SMA Treatment?

Being cared for in a top-ranked children’s hospital means your child will have immediate access to the many clinical specialists and pediatric-focused care they need to manage their SMA. We have the experts, support services, facilities and technology in place to ensure your child receives the best possible care.

It is our goal to deliver cutting-edge treatment to as many patients as possible. We have the resources required to provide access to new SMA therapies and medications in a timely manner. We are equipped to tailor dosing to each individual patient and provide the support services that can help make the experience easier on your child and family. These are important factors to look for in any SMA treatment center.

SMA Research:

While the approved therapies for SMA are limited at this time, there are many medications currently being studied with the hope that they may also become treatment options. CHOP has long been a site for research studies and clinical trials, continually seeking to find the next breakthrough in the treatment of SMA. In addition to interventional trials, we are a site for natural history studies that allow us to learn more about the disorder and how treatment is altering its natural history.