The Spinal Muscular Atrophy (SMA) Center is a multidisciplinary clinic at The Johns Hopkins Hospital.

Our Mission

• Provide expert and multidisciplinary care to patients with spinal muscular atrophy and related disorders, from infancy through adulthood.

• Administer new, FDA-approved treatments.

• Participate in multicenter clinical trials of novel SMA therapeutics.

• Offer support services to those living with SMA, as well as their families.

• Further understand the pathogenesis of SMA through integrating clinical and preclinical studies.

• Increase public awareness and educate patients and their families about SMA.

• Inspire and train the next generation of researchers and clinicians to address this devastating disorder.