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Mass General Spinal Muscular Atrophy (SMA) Multidisciplinary ClinicDepartment of Neurology
Charles River Plaza
165 Cambridge St
8th Floor, Neuromuscular Suite
Boston, Massachusetts, United States
The Mass General Spinal Muscular Atrophy (SMA) Multidisciplinary Clinic provides the latest treatments and research opportunities for people with Spinal Muscular Atrophy.
Find information, guides and more resources on each of the following topics to aid you in planning a SMA management strategy:
• Exercise & Mobility
• Special Considerations in SMA Infants
• Dental Care
The first medication for SMA, Spinraza (Nusinersen), was approved by the FDA in December 2016. We’re here to help answer any questions you may have about this new treatment for SMA. Other than Spinraza, medical care is primarily supportive, focused on respiratory support, nutritional support, and musculoskeletal management.
Coverage of Genetic Therapies for Spinal Muscular Atrophy Across Fee-for-Service Medicaid ProgramsBackground: Genetic therapies are a prom...
Patient of the Month: GiannaAfter noticing that her daughter was una...
STR1VE-EU Trial Shows Efficacy of Onasemnogene Abeparvovec in Spinal Muscular AtrophyOnasemnogene abeparvovec gene replacemen...
Parent Perceptions in Choosing Treatment for Infants With Spinal Muscular Atrophy Diagnosed Through Newborn Screenin...Objective: To identify factors parents c...
Implications of Circulating Neurofilaments for Spinal Muscular Atrophy Treatment Early In Life: A Case SeriesThis longitudinal cohort study aimed to ...
Axonal Excitability Changes in Children With Spinal Muscular Atrophy Treated With NusinersenSpinal muscular atrophy (SMA) is associa...
SMA: Considerations for Newborn Screening and Managementhttps://www.youtube.com/watch?v=FkshzHlc...