not yet recruiting

Antisense Oligonucleotide for Spinal Muscular Atrophy

key information

study id #: NCT05187260

condition: Spinal Muscular Atrophy

status: Not yet recruiting


This is a longitudinal, multiple-center, observational study of patients genetically confirmed chromosome 5q SMA to monitor the efficacy, safety, tolerability of SPINRAZA® (nusinersen) for up to 24 months.

intervention: Nusinersen


last updated: February 04, 2022