not yet recruiting

Pediatric SMA China Registry

key information

study id #: NCT05042921

condition: Muscular Atrophy, Spinal

status: Not yet recruiting


The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) treatments among pediatric chinese participants with spinal muscular atrophy linked to chromosome 5q (5q-SMA).


last updated: February 04, 2022