Pediatric SMA China Registry
study id #: NCT05042921
condition: Muscular Atrophy, Spinal
status: Not yet recruiting
purpose:The primary objective of the study is to describe the natural history and utilization of disease modifying therapy (DMT) treatments among pediatric chinese participants with spinal muscular atrophy linked to chromosome 5q (5q-SMA).
results: https://clinicaltrials.gov/ct2/show/results/NCT05042921
last updated: February 04, 2022
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