Trusted Resources: News & Meetings
Latest announcements and gatherings
18 resources available:
Dr John Brandsema Highlights Progress in SMA Treatment and Improved Outcomes for Patients
Source:
www.ajmc.com
Jul 19, 2022
Biohaven Enrolls First Patient in Phase 3 Trial of Taldefgrobep alfa in Spinal Muscular Atrophy (SMA)
Source:
www.prnewswire.com
Jul 7, 2022
Roche’s Evrysdi Offers Survival Benefits in Babies With SMA
Source:
www.clinicaltrialsarena.com
May 3, 2022
Biogen Announces New Updates Across Its SMA Research Program at 2022 MDA Conference
Source:
www.globenewswire.com
Mar 14, 2022
Will Parental Vaccine Hesitancy Retard the Embrace of Life-Saving Newborn Genetic Screening and Emerging Gene Therapy Revolution?
Source:
geneticliteracyproject.org
Jan 25, 2022
FDA Grants Evrysdi® Priority Review Based on Results From Treating Pre-Symptomatic Infants With Spinal Muscular Atrophy
Source:
www.prnewswire.com
Jan 25, 2022
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6 resources available:
Scholar Rock Provides Corporate Update and Highlights Priorities for 2022
Source:
www.businesswire.com
Jan 10, 2022
Biogen Exercises Option With Ionis to Develop and Commercialize Investigational ASO for SMA
Source:
www.biospace.com
Jan 4, 2022
Why Some Drugs Cost $2.1 Million per Dose and how one Company Plans to Change This
Source:
www.forbes.com
Dec 16, 2021
A Dallas Startup Aims to Build a Big Business—and Transform Lives—by Curing Rare Diseases
Source:
www.texasmonthly.com
Nov 1, 2021
Biogen to Launch Study of Higher Spinraza Dose in Patients With Later Onset SMA
Source:
www.healio.com
Sep 24, 2021
Cure SMA, Cytokinetics Renew Joint Efforts to Raise Funds and Awareness
Source:
smanewstoday.com
Sep 10, 2021
9 resources available:
Girl Born With Progressive Disease SMA on the Mend, Has Big Plans for the Future
Source:
www.cbsnews.com
Sep 13, 2022
A New Hip for a Patient With Rare Neuromuscular Condition
Source:
health.ucdavis.edu
Apr 22, 2022
New Treatment Can Help Fresno Infant With Rare Genetic Disorder
Source:
abc30.com
Jan 29, 2022
Springfield Second-Grader Attends Class From Home Through Double Robotics
Source:
www.springfieldnewssun.com
Jan 5, 2022
Artist With SMA Pens Song ‘SPACES’ About Looking Beyond Disability
Source:
hcp.smanewstoday.com
Dec 6, 2021
How One Mother Is Raising Awareness for Spinal Muscular Atrophy – A Leading Genetic Cause of Infant Death
Source:
storystudio.chron.com
Nov 30, 2021
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11 resources available:
The Orphan Drug Act Turns 40: NORD Celebrates Its Impact on Rare Diseases
Source:
rarediseases.org
Jan 4, 2023
SMA Screening Now Available to 87% of Newborns in US
Source:
smanewstoday.com
Jan 31, 2022
Study Highlights Gaps in Knowledge Among Prenatal Genetic Counselors
Source:
smanewstoday.com
Jan 28, 2022
Vitamin K Deficiency Caused Blood Clotting Problem in SMA Teen
Source:
smanewstoday.com
Jan 19, 2022
The Real Reason Some Newborns Don’t Get Screening for Deadly Diseases
Source:
www.medpagetoday.com
Dec 21, 2021
Newborn Screening, Treatment Make Big Difference With Rare Muscle Disorder
Source:
madison.com
Dec 20, 2021
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7 resources available:
2023 Annual SMA Conference
Source:
www.annualsmaconference.com
Jun 29, 2023
Rare Disease Day at NIH 2023
Source:
ncats.nih.gov
Feb 28, 2023
Rare Disease Week on Capitol Hill
Source:
everylifefoundation.org
Feb 28, 2023
Fighting for Kaiden Facebook Live: How Do I Promote an Active Lifestyle?
Source:
fightingforkaiden.org
Sep 27, 2022
6th Annual Faces of SMA Celebration & Silent Auction
Source:
www.eventbrite.com
Aug 13, 2022
Paul Reed Smith Guitar Model SE 24-08
Source:
www.eventbrite.com
Aug 13, 2022
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